
Novel translational readthrough-inducing препарат (TRID), rescuing the functional full-length protein expression in genetic diseases, such as cystic fibrosis, caused by premature termination codons (PTCs)
Novel translational readthrough-inducing drug (TRID), rescuing the functional full-length protein expression in genetic diseases, such as cystic fibrosis, caused by premature termination codons (PTCs)
Только для научно-исследовательского применения. Не предназначено для использования у пациентов или в качестве лекарственного средства.